The results from the first human trials for a Gene Therapy to treat patients with haemophilia A have just been published, and they are truly remarkable. The treatment has essentially cured almost all the participants, suggesting a transformative change is on the horizon in how this previously incurable genetic disease is treated.
- gene therapy
- The CRISPR controversy: Scientists skeptical over recent critical study
- CRISPR successfully removes genetic disease from human embryo
- Gene therapy could wipe immune memory and "turn off" severe allergies
- Landmark decision? US Supreme Court rules human genes cannot be patented
- Leukometer promises needle-free monitoring of the immune system
- "Genetic instruction manual" may unlock human limb regeneration