The results from the first human trials for a Gene Therapy to treat patients with haemophilia A have just been published, and they are truly remarkable. The treatment has essentially cured almost all the participants, suggesting a transformative change is on the horizon in how this previously incurable genetic disease is treated.
.. Continue Reading "Mind-blowing results" from gene therapy trial point to a cure for haemophilia
Category: Medical
Tags:
- Blood
- gene therapy
- Genetics
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