As an important drug modality, the development of oligonucleotides will continue to expand in the coming years. Oligonucleotide drugs are a class of therapeutic agents composed of short nucl… Read More

Introduction The report “Oligonucleotide Synthesis Market by Product (Drug, Synthesized Oligo (Primer), Reagents), Type (Custom, Predesigned), Application (Therapeutic (ASO, siRNA)… Read More

Advancing RNA-Targeted Therapies: A Phase 1 Clinical Perspective on Oligos and Beyond… Read More

Dziś Rampowiczka Agnieszka zaprasza do przeczytania rozmowy z bardzo ciekawym człowiekiem. Jest nim Artur, pracownik i podopieczny Fundacji Niesiemy Nadzieję. Artur ma zanik m… Read More

The most common congenital malformation of the central nervous system (CNS) is neural tube defects (NTDs). NTDs occur due to incomplete closure of the neural tube during embryonic… Read More

Un efecto positivo del tratamiento con nusinersen sobre la función motora en pacientes ambulatorios con atrofia muscular espinal (AME) pediátricos y adultos durante un per&iacu… Read More

A comprehensive research report on the Global Motor Neuron Diseases Treatment Market is a focused research compilation of all factors that can be considered critical for the evaluation of an… Read More

Small nucleic acid-based drugs, namely oligonucleotide drugs, are short-chain nucleic acids consisting of dozens of nucleotides in series. At present, most oligonucleotide drugs are obtained… Read More

The Spinal Muscular Atrophy Market report provides current treatment practices, emerging drugs, Spinal Muscular Atrophy market share of the individual therapies, current and forecasted Spin… Read More

Clinical research experts from the CRO Medpace shared insights about the operational and regulatory considerations for neuroscience trials with direct CNS administration. According to the Un… Read More

حقنة ضمور العضلات الشوكي، وأنو… Read More

Oligonucleotides are short synthetic DNA or RNA polymers, which modulate gene expression through Watson-Crick base pairing with targeted nucleic acids. Oligonucleotides regulate gene express… Read More

Drug Modification Drug modification involves altering the chemical structure of the drug itself (such as functional groups, amino acids or nucleic acid skeletons) and coupling the drug wi… Read More

With the continuous development of molecular biology technology, the relationship between gene mutations and diseases has gained more and more in-depth understanding. Nucleic acids have attr… Read More

Nusinersen wszedł do lecznictwa w grudniu 2016 roku i był pierwszym lekiem zatwierdzonym do leczenia rdzeniowego zaniku mięśni. Agata Rocznika została zakwalifikowan… Read More

Nucleic acid and nucleic acid drugs Nucleic acid is the carrier of life genetic information. It has both the storage function of life information and the active function of biocatalysis… Read More

Novartis’ Zolgensma (onasemnogene abeparvovec) gene therapy has been making significant strides as of late, including dosing of the first Spinal Muscular Atrophy (SMA) patient with the… Read More

Sağlık Bakanı Fahrettin Koca SMA Bilim Kurulu’nun toplantı yaptığını açıkladı. Bakan Koca sosyal medya hesabından; “… Read More

A 1-year-old Russian girl suffering from a rare neuromuscular disease has received an injection of what’s been dubbed the world’s “most-expensive shot,” th… Read More

The second-ever gene therapy received US Food and Drug Administration (FDA) approval last Friday, giving hope to infants with a severe form of spinal muscular atrophy (SMA), a devastating ge… Read More

La compañía farmacéutica Biogen, administradora de la Spinraza (Nusinersen) en Estados Unidos le aseguró a la niña cubana diagnosticada con el Síndr… Read More

Новое лечение болезни Хантингm… Read More

Biogen Inc.  today reported first quarter 2016 financial results, including: Total revenues of $2.7 billion, a 7% increase versus the same period in the prior year. Growth was driven b… Read More